Something common to most strategies with viruses is the need to use “packaging” cell lines or helper viruses, which carry the genes that we eliminate to our vectors and that allow infection. Supporters believe that the treatment is messing with the unknown. GAVIN THOMAS Of course, once more testing is conducted, we will know more about this treatment in terms of efficacy and side effects. Improving your life knowledge health and family. The somatic gene therapy is so far the one that has dissimilar applications in a few diseases such as: Cystic fibrosis, Lysosomal diseases, hypercholesterolemia, malignant melanomas (cancer), Severe Combined Immune Deficiency, Duchenne Muscular Dystrophy, Beta Thalassemia, HIV / AIDS, among others. Gene Therapy 101: Fast Facts & FAQ’s Gene Therapy 101: Fast Facts & FAQ’s. Something common to most strategies with viruses is the need to use “packaging” cell lines or helper viruses, which carry the genes that we eliminate to our vectors and that allow infectionSome types of viruses insert their genes physically in the genome of the host, others pass through several cellular organelles in their cycle of infection and others replicate directly in the cytoplasm, so depending on the therapy to perform we may be interested in one or the other . Gene therapy could also introduce a healthy gene to make the body resistant to diseases. As mentioned above, gene therapy remains at the experimental stage. 11111 Fact Sheet 23 |GENE THERAPY 1 1 Page 1 of 2 www.genetics.edu.au Updated 30 September 2015 This fact sheet describes gene therapy as it is used to treat medical conditions and the benefits and challenges it raises. February 3, 2016 GAVIN THOMAS Learn Gene therapy facts for kids. Gene therapy means putting in a working gene to a person who has a damaged gene. Due to the deficiencies of many of the gene transfer systems, some hybrid methods have been developed that combine two or more techniques. Course of Introduction to Biotechnology. August 7, 2019, 7:08 pm, by October 17, 2019, 2:14 am, by Modern medicine has come a long way. Some examples are retroviruses, adenoviruses, adeno-associated viruses, herpes viruses and viral vectors. to be introduced. Gene therapy is a type of alternative healing technique that uses a patient’s own genes to treat or prevent a certain disease. The European Commission has approved this method for one particular treatment. 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